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Principles and Practices of Gene Therapy

Wednesday, January 14, 2015
Course topic: 

Course Description

Gene therapy is promising to be key in the battle against cancer, inherited disorders, and many other diseases. Decades worth of advances in this field have resulted in a growing number of successful clinical trials to develop safe and effective treatments. Over the past few years scientists have developed a number of new nucleic acid-based therapies, which continue to improve the versatility of these genetic-based treatment approaches. In this course, you will start by building a fundamental understanding of gene therapy, then dive deeper with an in-depth look at important trends, research and advances in gene therapy. You will gain a clear understanding of how gene therapy works, how it has developed and advanced, and how much potential it has.

You will learn

  • Basic principles for getting nucleic acids into cells and using viruses to transfer DNA
  • Proven and new approaches to clinical trials
  • How to effectively use genome editing tools
  • Methodologies for successful RNAi and expression of non-coding RNAs to regulate genes and treat disease

Please note: This course is an elective course in the Stanford Genetics and Genomics Certificate.*

*This certificate neither substitutes for, nor leads to, being board certified as a genetic counselor (ABGC) or clinical geneticist (ABMG)